Draft

262  Sleep Jc Sept 2022

262.1 Summary

  • Sleep Journal Club
  • Goals:
  • Imagine it’s 1950. You discover that OSA is very common. How do you figure out if it matters?
  • Structure of Observational Study ‘Argument’: Disjunctive Syllogism
  • Association of obstructive sleep apnea with all-cause andcardiovascular mortality: A population-based study
  • Statistical Teaching point:
  • Design: Retrospective Cohort Cross-sectional
  • Cross-sectional vs Retrospective Cohort
  • Obstructive Sleep Apnea as a Risk Factor for Stroke and Death
  • Community vs Clinical Cohort
  • Prospective Study of Obstructive Sleep Apnea and Incident Coronary Heart Disease and Heart FailureThe Sleep Heart Health Study
  • Confounders, Regressions

262.2 Slide outline

262.2.1 Slide 1

  • Sleep Journal Club
  • Sept 3 2022 ### Slide 2
  • Goals:
  • Understand that the disjunctive syllogism is the structure of a scientific argument
  • Know the limitations of a cross-sectional design as compared to cohort as compared to randomized trial viz-a-viz causal inference
  • Understand what a hazard ratio is and why they are so common in medical research
  • Know the determinants of a studies power. ### Slide 3
  • Imagine it’s 1950. You discover that OSA is very common. How do you figure out if it matters? ### Slide 4
  • Structure of Observational Study ‘Argument’: Disjunctive Syllogism ### Slide 5
  • TODO: No text extracted from this slide. ### Slide 6
  • Association of obstructive sleep apnea with all-cause andcardiovascular mortality: A population-based study
  • Design: Retrospective Cohort
  • Population: NHANES (multistage-sampling survey) 2005-8 who had OSA status and CV status known (9000 pt)
  • Exposed: Yes to ”Have you been told you have a sleep problem: OSA”
  • Unexposed: no to the above
  • Outcome: Prevalent HTN, CV disease; Incident CV-death and mortality
  • Statistics: Logistic (yes/no) and Cox (Hazard Ratio) regressions accounting for demographics, health status.
  • Findings: Prevalent HTN+CV indep assoc, CV-death and mort not ### Slide 7
  • Statistical Teaching point:
  • Ascertainment of exposure status
  • Is “Have you ever been diagnosed with OSA?” accurate?
  • How would you expect the group assignment to change if PSG was used?
  • If you could design a perfect categorization of the groups, what would it be?
  • How would this effect the study conclusions? ### Slide 8
  • TODO: No text extracted from this slide. ### Slide 9
  • Design: Retrospective Cohort Cross-sectional
  • Population: Sleep Heart Health (1995-98), n6424 (-1200 missing data)
  • Exposed/Unexposed: AHI quartile (0-1.3, 1.4-4.4, 4.5-11.0, 11+)
  • Also, Sleep hypoxemia and arousal index
  • Outcome: Prevalent odds of CVD (why not incident?)
  • Statistics: Logistic regression with possible confounders
  • Findings: Quartile III and IV of AHI and %Hypoxemia indepdently associated with prevalent CVD (particularly HF and Stroke).
  • Sleep-disordered Breathing and Cardiovascular DiseaseCross-sectional Results of the Sleep Heart Health Study ### Slide 10
  • Cross-sectional vs Retrospective Cohort
  • Cross-sectional study: exposure and outcome assess simultaneously
  • Cohort study: exposure assessed before outcome
  • Can only investigate prevalence of disease
  • Pros: easy, reliable if exposure doesn’t change (eg genetics), or prior exposure hard to remember (eg diet)
  • Cons: can’t determine direction of causality, current exposuresurrogate for past exposure, overrepresent longer duration cases. ### Slide 11
  • TODO: No text extracted from this slide. ### Slide 12
  • Obstructive Sleep Apnea as a Risk Factor for Stroke and Death
  • Design: Prospective cohort (clinical)
  • Population: W/o pre-existing CVD referred for SDB eval @ Yale. 1997-2000, n1022
  • Exposed: Referred to clinic, AHI > 5 events/hr
  • Unexposed: Referred to clinic, AHI < 5 events/hr
  • Outcome: incident stroke or death, median follow-up 3.4 yr
  • Statistics: Cox-regression~Kaplan Meier/Log rank/proportional hazard
  • Findings: OSA associated with HR 1.97 for stroke or death after adjusting for confounders ### Slide 13
  • Community vs Clinical Cohort
  • Community comparison:
  • (C+D) vs A
  • Clinical comparison:
  • C vs B
  • Any factor that changes the likelihood of B+C is a potential confounder
  • If, rather than population burden, you are interested in how to care for B+C, this may be the correct method
  • Population of interest
  • Seeks care
  • Has OSA
  • A
  • B
  • C
  • D ### Slide 14
  • TODO: No text extracted from this slide. ### Slide 15
  • Prospective Study of Obstructive Sleep Apnea and Incident Coronary Heart Disease and Heart FailureThe Sleep Heart Health Study
  • Design: Prospective cohort (community)
  • Population: Sleep Heart Health (1995-98), n6441 (-2000 excluded))
  • Exposed: Mild (5-15), Moderate(15-30), Severe (30+) OSA by AHI. Mostly untreated (2.1% overall, 8.4% w mod-sev OSA treated)
  • Unexposed: AHI < 5 events/hr
  • Outcome: incident CHD before 4/1/06 (~8.7y)
  • Statistics: Cox-regression (HR)
  • Findings: More severe OSA independently associate with incident CHD (particularly CHF) in men, not women. ### Slide 16
  • Confounders, Regressions
  • Regression: estimate effect with “all other things held equal”.
  • How do you decide what things to include?
  • Confounders
  • Mediators?
  • Colliders?
  • Is your understanding of what factors matter correct?
  • Can you measure everything you want to measure? ### Slide 17
  • TODO: No text extracted from this slide. ### Slide 18
  • Sleep-Disordered Breathing and Mortality: A Prospective Cohort Study
  • Design: Prospective cohort (community)
  • Population: Sleep Heart Health (1995-98), n6441 (-147 excluded d/t OSA treatment)
  • Exposed: Mild (5-15), Moderate(15-30), Severe (30+) OSA by AHI. Mostly untreated (2.1% overall, 8.4% w mod-sev OSA treated)
  • Unexposed: AHI < 5 events/hr
  • Outcome: (incident) death w/ ~8.2y avg follow-up
  • Statistics: Cox-regression (HR)
  • Findings: Mod-severe OSA (men) and severe OSA (women) associated with increased hazard of mortality. No relationship if age 70+ ### Slide 19
  • What is a Hazard Ratio / KM / Cox-regression?We’re all dead in the long run
  • 2 versions of Russian Roulette
  • X: 1:6 w/ bullet, Y: 1:4 w/ bullet
  • HR (1/6) / (1/4) 0.67
  • 1000 people play 11 rounds of each
  • On round
  • P(Surviving 10 rounds?)
  • X: (5/6)^10 16% -> 160 survivors
  • Y: (3/4)^10 5.6% -> 56 survivors
  • RR would be 84% / 94.6% 0.88
  • Round 11: X 27 die, Y 14 die yet HR higher in group Y!
  • What if Group Y says screw it after 7 rounds, but we want to maximize our data?
  • HR allows for “censoring of data” ### Slide 20
  • TODO: No text extracted from this slide. ### Slide 21
  • Effect of continuous positive airway pressure therapy on recurrence of atrial fibrillation after pulmonary vein isolation in patients with obstructive sleepapnea: A randomized controlled trial
  • Design: Open-label RCT (A3 study, Oslo)
  • Population: new dx AHI 15+, ESS < 15 (etc), undergoing CA-PVI for Afib and able to tolerate CPAP during run-in period
  • Exposed: randomized to auto-CPAP
  • Unexposed: randomized to no CPAP
  • Outcome: 2+min Afib months 3-12 after CA-PVI by loop recorder
  • Statistics: logistic-regression yes/no recurrence
  • Findings: Mod-severe OSA (men) and severe OSA (women) associated with increased hazard of mortality. No relationship if age 70+ ### Slide 22
  • Negative RCT after positive observational study? power, adherence, & confounding
  • Power ~ Sample size/$$$, Alpha, minimally important absolute effect size, info per data point (Continuous > HR > dichotomous), non-adherence/loss f/u
  • ?
  • Disease+
  • Hypothesis+
  • Disease-
  • Hypothesis-
  • Test+
  • Study+
  • TP
  • FP
  • PPV: TP / T+
  • Test –
  • FN
  • TN
  • NPV: TN / T-
  • Se: TP / D+
  • Power: Se
  • Sp: TN / D-
  • Alpha: 1-Sp ### Slide 23
  • TODO: No text extracted from this slide. ### Slide 24
  • Why do phase 2 trials: Why surrogates? Why process measures?
  • Need to estimate each of the above parameters
  • Surrogates: Chosen to show a larger effect size smaller trial
  • Validity depends on them correlating with the outcome of interest
  • Do NOT trust a positive clinical-outcome on a phase 2 trial powered to find a difference in a surrogate: increased error rates (Type 1 and 2)
  • Power ~ Sample size/$$$, Alpha, minimally important absolute effect size, info per data point (Continuous > HR > dichotomous), non-adherence/loss f/u ### Slide 25
  • Goals:
  • Understand that the disjunctive syllogism is the structure of a scientific argument
  • Know the limitations of a cross-sectional design as compared to cohort as compared to randomized trial viz-a-viz causal inference
  • Understand what a hazard ratio is and why they are so common in medical research
  • Know the determinants of a studies power.

262.3 Learning objectives

  • Sleep Journal Club
  • Goals:
  • Imagine it’s 1950. You discover that OSA is very common. How do you figure out if it matters?
  • Structure of Observational Study ‘Argument’: Disjunctive Syllogism
  • Association of obstructive sleep apnea with all-cause andcardiovascular mortality: A population-based study

262.4 Bottom line / summary

  • Sleep Journal Club
  • Goals:
  • Imagine it’s 1950. You discover that OSA is very common. How do you figure out if it matters?
  • Structure of Observational Study ‘Argument’: Disjunctive Syllogism
  • Association of obstructive sleep apnea with all-cause andcardiovascular mortality: A population-based study

262.5 Approach

  1. TODO: Outline the initial assessment or decision point.
  2. TODO: Outline the next diagnostic or management step.
  3. TODO: Outline follow-up or escalation criteria.

262.6 Red flags / when to escalate

  • TODO: List red flags that require urgent escalation.

262.7 Common pitfalls

  • TODO: Capture common errors or missed steps.

262.8 References

TODO: Add landmark references or guideline citations.

262.9 Slides and assets

262.10 Source materials